Experience

Rare Disease

  • HIV 1
  • Essential thrombocytosis
  • hemophilia a,b
  • Becker muscular dystrophy
  • chronic myeloid leukemia
  • Mucopolysaccharidosis
  • multiple myeloma
  • amyotrophic lateral sclerosis
  • Idiopathic thrombocytopenic purpura
  • acromegaly
  • Turner syndrome
  • Idiopathic short stature
  • Neuroblastoma
  • Myelodysplastic Syndromes
  • Chronic Myelogenous Leukemia
  • Growth hormone deficiency